Uncovering Genomic Causes of Co-Morbidity in Epilepsy: Gene-Driven Phenotypic Characterization of Rare Microdeletions

نویسندگان

  • Dalia Kasperavičiūtė
  • Claudia B. Catarino
  • Krishna Chinthapalli
  • Lisa M. S. Clayton
  • Maria Thom
  • Lillian Martinian
  • Hannah Cohen
  • Shazia Adalat
  • Detlef Bockenhauer
  • Simon A. Pope
  • Nicholas Lench
  • Martin Koltzenburg
  • John S. Duncan
  • Peter Hammond
  • Raoul C. M. Hennekam
  • John M. Land
  • Sanjay M. Sisodiya
چکیده

BACKGROUND Patients with epilepsy often suffer from other important conditions. The existence of such co-morbidities is frequently not recognized and their relationship with epilepsy usually remains unexplained. METHODOLOGY/PRINCIPAL FINDINGS We describe three patients with common, sporadic, non-syndromic epilepsies in whom large genomic microdeletions were found during a study of genetic susceptibility to epilepsy. We performed detailed gene-driven clinical investigations in each patient. Disruption of the function of genes in the deleted regions can explain co-morbidities in these patients. CONCLUSIONS/SIGNIFICANCE Co-morbidities in patients with epilepsy can be part of a genomic abnormality even in the absence of (known) congenital malformations or intellectual disabilities. Gene-driven phenotype examination can also reveal clinically significant unsuspected condition.

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عنوان ژورنال:

دوره 6  شماره 

صفحات  -

تاریخ انتشار 2011